Topic: genetic mutations
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Crispr Pioneer Launches Startup for Custom Gene-Editing Therapies
Aurora Therapeutics, co-founded by CRISPR pioneer Jennifer Doudna, aims to scale personalized gene-editing treatments for rare diseases using a novel FDA regulatory pathway that allows approval based on data from a small number of patients. The company's initial focus is on phenylketonuria (PKU),...
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The Future of Gene Editing: Curing Disease Without Limits
David Liu announced a new disease-agnostic gene-editing strategy that could treat multiple unrelated illnesses using a unified molecular framework. Current gene therapies are expensive and tailored to rare conditions, whereas Liu's approach aims to be a universal, scalable platform for broader ap...
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